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Gene profile

GNPAT

HGNC:4416 · SaudiVarKB evidence summary derived from retained literature mentions.

2Gene mentions
2Publications
2Linked variants
4Associated phenotypes

Associated phenotypes

Co-mentioned in GNPAT publications
PhenotypeIdentifierArticlesMentions
intellectual disabilityHP:000124911
epilepsyHP:000125011
skeletal dysplasia11
congenital cataract11

Linked variants

Variants normalized to GNPAT
VariantHGVS / rsIDArticlesMentions
c.1602+1G>Ac.1602+1G>A11
g.231408138G>Ag.231408138G>A11

Population context

Reported in the same publications
Country / regionGroupCohortArticles
Not specified161

Supporting publications

2 records
  1. 2023Neonatal rhizomelic chondrodysplasia punctata type 2 caused by a novel homozygous variant in the GNPAT gene.Clinical case reportsPubMed ↗
  2. 2021Clinical, biochemical, and molecular characterization of mild (nonclassic) rhizomelic chondrodysplasia punctata.Journal of inherited metabolic diseasePubMed ↗